Yannick, 13, was blind before receiving gene therapy, which restored much of his sight.
Dr. Katherine High has pioneered the development of gene therapy for nearly two decades.
Gene therapy is giving Michael, 67, new hope for a life free from hemophilia B.
The team at Spark Therapeutics has pioneered the development of gene therapy for nearly two decades. Our founding team has brought us closer to solving the most complex challenges facing the field, creating new opportunities for the patients we serve and for the industry at large. Learn how we’re working to spark the next wave in the gene therapy revolution. Read on
Spark and Genable Technologies recently announced a collaboration agreement that will draw on Spark’s deep expertise in the clinic and in AAV manufacturing to advise on the development of GT038, Genable’s preclinical ocular gene therapy.