Yannick, 13, was blind before receiving gene therapy, which restored much of his sight.
Dr. Katherine High has pioneered the development of gene therapy for nearly two decades.
Gene therapy is giving Michael, 67, new hope for a life free from hemophilia B.
Spark to open permanent west Philadelphia headquarters.
The team at Spark Therapeutics has pioneered the development of gene therapy for nearly two decades. Our founding team has brought us closer to solving the most complex challenges facing the field, creating new opportunities for the patients we serve and for the industry at large. Learn how we’re working to spark the next wave in the gene therapy revolution. Read on
Biopharmaceutical industry leaders Vin Milano and Lars Ekman recently joined the Spark board of directors. Their expertise in the field will bring valuable guidance as Spark continues to progress their lead program, a Phase 3 study for RPE65-related blindness.